pe
pep-10450 v1 CC-BY-SA-4.0

Substance P receptor blocker (CHEMBL2369630)

A lab-made ring-shaped peptide that blocks the substance P receptor, which helps carry pain and nausea signals; used only as a research tool.

statusbioassayed targetTACR1 length12 aa refs1
status 5 / 5
prediction metrics boltz-2 2.2.1
ipTM0.976
pTM0.934
avg pLDDT68.4
ranking score0.742
STRUCTURE · PEP-10450 × TACR1
ranking0.742
target interface 4.5Å peptide drag rotate · ctrl+scroll zoom · right-click pan
boltz-2 2.2.1 · mmCIF ↓ download
sequence12 aa
151012
GACKNFFWTFTS
in the news 1 article
overview readme

What this is

CHEMBL2369630 is a synthetic cyclic peptide designed as an antagonist of the NK1 receptor (also called the substance P receptor, encoded by TACR1). It belongs to a line of research that asked whether the backbone scaffold of somatostatin — a naturally cyclic, disulfide-bridged peptide — could be repurposed to block substance P rather than mimic it. The result is a 14-residue ring that competes with substance P for the NK1 receptor binding site with an IC50 of 44 nM in cell-based radioligand displacement assays, as reported by Liu and colleagues (Journal of Medicinal Chemistry, 2000).

The stored sequence GACKNFFWTFTS is a simplified 12-residue representation. The actual compound is a 14-residue cyclic peptide in which Cys at position 3 forms a disulfide bridge with a D-Cys residue at position 14, and position 9 carries a fluorinated non-canonical amino acid — neither the ring closure nor the modified residue is visible in the stored sequence.

History

The conceptual lineage of CHEMBL2369630 runs through two converging threads. The first is the tachykinin field itself: substance P was identified in 1931 by von Euler and Gaddum as an intestinal-contracting extract, its eleven-amino-acid sequence was determined in 1971, and by 1984 the community had agreed to name its three receptor subtypes NK1, NK2, and NK3 (Garcia-Recio and Gascón, BioMed Research International, 2015; Hökfelt and colleagues, Journal of Internal Medicine, 2001). Peptide antagonists derived directly from substance P's sequence emerged in the 1980s, but they suffered from poor selectivity, limited potency, and unfavorable pharmacokinetics.

The second thread is the somatostatin scaffold program. Somatostatin is itself a disulfide-cyclized peptide, and researchers including Hirschmann and Smith at the University of Pennsylvania, in collaboration with Merck Research Laboratories, had spent the preceding decade exploring whether its ring structure could serve as a geometry-fixing scaffold for diverse pharmacological activities. Liu and colleagues (Journal of Medicinal Chemistry, 2000) reported the culmination of that effort as applied to NK1 antagonism: by grafting substance P pharmacophore elements onto the somatostatin backbone they obtained a compound — CHEMBL2369630 — whose agonist-vs-antagonist behavior and receptor subtype selectivity they analyzed in terms of pseudosymmetry within the scaffold.

What it does

CHEMBL2369630 competes with substance P for binding to the NK1 receptor, displacing the radioligand [¹²⁵I]substance P from cells expressing TACR1 with IC50 = 44 nM. It also shows measurable, weaker affinity at the NK2 receptor (TACR2; IC50 = 730 nM in the same cell-based format), making it roughly 17-fold selective for NK1 over NK2 (Liu and colleagues, 2000, via ChEMBL bioactivity records).

The NK1 receptor is a G protein-coupled receptor expressed widely in the central and peripheral nervous system. Substance P binding to NK1 contributes to nociceptive signaling, the vomiting reflex, and neuromodulation; receptor antagonism at NK1 is the mechanism exploited by aprepitant, the FDA-approved antiemetic for chemotherapy-induced nausea (Garcia-Recio and Gascón, BioMed Research International, 2015).

Evidence

  • Human: No human trials. CHEMBL2369630 is a research ligand characterised exclusively in biochemical and cell-based assays; no in vivo studies are recorded in the source publication or ChEMBL bioactivity database.
  • Animal: None reported for this compound.
  • In vitro: Radioligand displacement assays in CHO cells expressing human TACR1 or TACR2 yielded IC50 = 44 nM (NK1) and IC50 = 730 nM (NK2). Extended mutagenesis assays in COS cells with the same radioligand showed that substituting histidine residues in the NK1 receptor substantially reduced binding (IC50 shifted to 2700–8200 nM for H197A and H265A mutants), and the Q165A mutation also reduced affinity (IC50 = 3600 nM), indicating that these extracellular positions contribute to the peptide-binding site (Liu and colleagues, Journal of Medicinal Chemistry, 2000, via ChEMBL bioactivity records).

Mechanism

CHEMBL2369630 acts as a competitive antagonist at TACR1, the primary substance P receptor. Substance P makes key contacts at the extracellular loops and outer transmembrane helices of NK1; the conserved C-terminal Phe-X-Gly-Leu-Met-NH₂ motif of tachykinins drives receptor engagement, while the N-terminal sequence provides selectivity between NK1 and NK2 (Madsen and colleagues, Journal of Biological Chemistry, 2023). Peptide antagonists of NK1 compete at this same extracellular binding surface — a different pocket from the transmembrane cavity occupied by small-molecule antagonists such as aprepitant.

The somatostatin scaffold constrains the backbone into a geometry that presents the substance P pharmacophore elements without triggering full agonism. Liu and colleagues (2000) analyzed the agonism-vs-antagonism outcome in terms of pseudosymmetry: the disulfide-bridged ring of somatostatin has approximate twofold symmetry, and the orientation of grafted pharmacophore groups relative to that axis determines whether the resulting compound activates or blocks the receptor. The mutagenesis data (Q165A, H197A, H265A NK1 mutants losing 30- to 190-fold in affinity) localise the compound's contact surface to the outer receptor face.

Known effects

  • NK1 (TACR1) antagonism — In vitro; IC50 = 44 nM (CHO cell radioligand displacement assay, Liu and colleagues, 2000)
  • NK2 (TACR2) binding — In vitro, weaker; IC50 = 730 nM (same format)
  • Receptor contact-site mapping — Mutagenesis assays identify Q165, H197, H265 on NK1 as binding determinants

Regulatory status

  • Research compound only. No regulatory submissions; no IND, NDA, or EMA filing on record.
  • Not approved for any human use.

Related peptides

The somatostatin scaffold program that produced this compound intersects with several other NK1-active and GPCR-active cyclic peptides on the platform. Substance P itself (the endogenous NK1 agonist whose binding this compound blocks) is the direct pharmacological counterpart. The clinically approved NK1 antagonist aprepitant (MK-869) works by the same receptor-blocking mechanism but uses a small-molecule rather than a peptide scaffold.

Hypotheses4 directions▾ collapse

Research directions for this peptide, selected from the current sources — hypotheses you can explore and model. None of it is proven yet; tap any one to see the full thinking.

openupdated 2026-06-11

Could this cyclic peptide work as a pain treatment by blocking substance P signals in peripheral tissues while staying outside the brain?

Existing NK1-blocking drugs that enter the brain failed for depression and had mixed results in pain. A peptide version that stays out of the brain might deliver pain relief for conditions like migraines or IBS while avoiding those earlier pitfalls, giving patients a safer option.

The hypothesis
CHEMBL2369630 has latent antinociceptive activity in neuroinflammatory pain models mediated by peripheral NK1 blockade that is independent of CNS penetration, because its cyclic, disulfide-bridged scaffold and moderate size (~1.5 kDa) restrict blood-brain barrier passage while still reaching NK1-expressing dorsal root ganglion neurons and mast cells in peripheral tissue.
Why it’s plausible
Substance P and NK1 drive peripheral sensitization and mast cell degranulation in pain conditions including migraine, IBS, and rheumatoid arthritis. CNS-penetrant NK1 antagonists (aprepitant) failed in depression and anxiety trials partly because peripheral vs. central contributions were conflated. A peripherally restricted NK1 antagonist would be valuable for pain without CNS liability. The peptide's size and polarity profile make CNS exclusion likely, and peripheral NK1 biology is clinically validated.
Why it matters
A peripherally restricted NK1 antagonist derived from this scaffold would be testable in models of neurogenic inflammation without CNS liability, and could be repurposed for pain indications that eluded CNS-penetrant NK1 drugs in failed clinical trials.
Plausibility.60
Novelty.55
Impact.65
Basis · grounding3 computed/notes
[1]
noteCompound is a ~1.5 kDa cyclic disulfide-bridged peptide; such molecules are generally excluded from the CNS, making peripheral NK1 biology the relevant pharmacological compartment.
[2]
noteTargets annotated as TACR1 and TACR2, both expressed on peripheral sensory neurons (DRG) and mast cells where neurogenic inflammation is initiated by substance P.
[3]
sequenceSequence GACKNFFWTFTS is 12 residues with multiple aromatic and polar residues; high MW and polarity predict low passive transcellular permeability at the blood-brain barrier.
openupdated 2026-06-11

Could grafting a somatostatin signal onto the free end of this peptide create a single drug that blocks pain-driving inflammation and slows neuroendocrine tumor growth?

If this design works, patients with neuroendocrine tumors could receive a single peptide drug addressing both the tumor and the pain, replacing a two-drug regimen with one more manageable treatment.

The hypothesis
The somatostatin-derived ring scaffold of CHEMBL2369630 can be engineered to carry a third pharmacophore grafted at the GACK N-terminal flap to simultaneously antagonize TACR1 while agonizing the somatostatin receptors (SSTR2/SSTR5), creating a bifunctional peptide that co-suppresses neurogenic inflammation and somatostatin-sensitive tumor growth in the same molecule.
Why it’s plausible
The compound was designed by repurposing somatostatin's disulfide-constrained ring onto a tachykinin pharmacophore. Somatostatin and its analogs (octreotide, lanreotide) are clinically validated SSTR2/5 agonists. The GACK N-terminal segment diverges from the somatostatin pharmacophoric core (FWKT) and is not the contact zone for NK1, so it is a candidate insertion point. Dual NK1/SSTR pharmacology would be novel: NK1 drives neurogenic inflammation in many tumors, while SSTR2 suppresses neuroendocrine growth.
Why it matters
A single molecule that blocks substance P-driven inflammation and activates somatostatin tumor suppression would address two complementary mechanisms in neuroendocrine cancers and inflammatory pain without requiring combination therapy.
Plausibility.45
Novelty.75
Impact.70
Basis · grounding3 computed/notes
[1]
noteExplicit statement that the somatostatin disulfide-bridged cyclic scaffold was repurposed to block NK1, establishing structural homology and suggesting the core ring tolerates NK1-oriented substitution without losing scaffold integrity.
[2]
sequenceGACKNFFWTFTS: the NFFWTF segment mirrors the somatostatin pharmacophore (FWKT numbering); GACK is a free N-terminal segment likely tolerant of substitution without disrupting the disulfide.
[3]
structureHigh ipTM (0.976) for NK1 complex suggests the FFWTF core is the binding determinant, implying the N-terminal GACK flap is available for pharmacophore addition.
openupdated 2026-06-11

Does this cyclic peptide bind the NK1 receptor deep in the transmembrane pocket, like small-molecule drugs do?

Mutating three pocket residues (Gln165, His197, His265) already weakens this peptide's binding, the same residues that small-molecule NK1 blockers need. Confirming a shared pocket would help explain why oral NK1 blockers work and guide peptide-based treatments for nausea or pain.

The hypothesis
The very high Boltz-2 ipTM (0.98) for CHEMBL2369630 binding TACR1 reflects engagement with the conserved transmembrane orthosteric pocket shared by small-molecule NK1 antagonists, meaning the cyclic peptide occupies a GPCR site geometry more typically exploited by small molecules than by peptides.
Why it’s plausible
Boltz-2 ipTM of 0.976 is unusually high for a peptide-GPCR complex, suggesting a well-defined, buried binding pose rather than a surface interaction. The literature snippet explicitly references a 'Common Binding Site for Small Molecules Within the Transmembrane Domain of G-Protein Coupled Receptors,' and the compound's synthetic, constrained scaffold would be compatible with a transmembrane pocket. If confirmed, CHEMBL2369630 bridges peptide and small-molecule NK1 pharmacology.
Why it matters
If this peptide engages the same transmembrane pocket as oral NK1 antagonists (aprepitant class), it would validate cyclic peptide scaffolds as transmembrane GPCR binders, opening a new design space for cyclic peptide CNS/nausea drugs.
Plausibility.85
Novelty.25
Impact.60
Basis · grounding1 paper · 2 computed/notes
[1]
structureBoltz-2 ipTM = 0.9764 indicates very high predicted interface confidence, consistent with buried transmembrane binding rather than loose surface contact.
[2]
paper
Paper references a common transmembrane binding site for small molecules in GPCRs, directly relevant to the NK1 receptor occupied by this compound.
doi: 10.1021/jm000316h
[3]
noteIC50 = 44 nM in radioligand displacement assay confirms direct competition at the substance P binding site on NK1.
openupdated 2026-06-11

Is the N-terminal segment outside the disulfide ring required to mold itself around the receptor's outer loop?

A moderate model-confidence score hints (but does not prove) the tail is flexible. If experiments show that flexibility is load-bearing for binding, designers would know not to rigidify it in next-generation analogs, avoiding failed optimization.

The hypothesis
The moderate pLDDT (68.4) of the bound complex reflects conformational flexibility of the disulfide-constrained ring at the N-terminal GACK segment, and this local disorder is functionally necessary because it enables an induced-fit interaction with the flexible extracellular loop 2 of TACR1 upon receptor engagement.
Why it’s plausible
Boltz-2 ipTM is very high (0.976) but pLDDT is only 68.4, indicating that the complex interface is well-defined while part of the peptide itself remains locally disordered in the predicted structure. The GACK N-terminal segment precedes the disulfide-forming Cys and the pharmacophoric FFWTF core. In cyclic peptide-GPCR structures, extracellular loop 2 (ECL2) frequently undergoes induced-fit remodeling. Local disorder at GACK could allow ECL2 engagement that rigidifies only upon binding.
Why it matters
Knowing which segment is flexible in solution versus rigid in complex guides scaffold optimization: if GACK disorder is needed for ECL2 contact, over-constraining that segment would abolish potency, while grafting the rigid FFWTF core onto a more metabolically stable scaffold could preserve it.
Plausibility.40
Novelty.55
Impact.45
Basis · grounding3 computed/notes
[1]
structurepLDDT = 68.4 alongside ipTM = 0.976 implies locally disordered peptide regions that resolve on binding; the GACK N-terminal segment is the most chemically flexible portion before the disulfide anchor.
[2]
sequenceSequence GACKNFFWTFTS: Gly-Ala-Cys (positions 1-3) is the flexible linker region preceding the aromatic pharmacophore NFFWTF; Gly is a known disorder-promoting residue.
[3]
noteThe ring is closed by a disulfide between Cys-3 and D-Cys-14; the intervening segment forms the constrained macrocycle, but the exact geometry of the N-terminal GACK flap is not fixed by the disulfide alone.
details expand to inspect
full evidence table1 metrics
metricvaluetool
IC50 44 nM GPCRDB/ChEMBL
3-letter notation
Gly-Ala-Cys-Lys-Asn-Phe-Phe-Trp-Thr-Phe-Thr-Ser
recipeboltz-2 2.2.1
parametervalue
modelboltz-2 2.2.1
weights
hardwarevast_v100_32gb
mlx version
python
random seed1
msa strategycolabfold_local
runtime
predicted by
predicted at2026-05-22
citationbibtex
peptidemodel (2026). Substance P receptor blocker (CHEMBL2369630) (pep-10450, v1). PeptideModel. https://peptidemodel.com/card/pep-10450
@peptide{pep10450,
  sequence = {GACKNFFWTFTS},
  target   = {tacr1},
  author   = {peptidemodel},
  year     = {2026},
  status   = {bioassayed}
}
related peptides 3 by signal overlap
clinical trials 0 trials · checked 2026-05-22
0
no registered clinical trials as of 2026-05-22; we'll re-check periodically
references 1 papers
discussion no comments
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peptidemodel.com CC-BY-SA-4.0 research only · not for human use